Clinical manifestation, disease course and response to enzyme replacement therapy in Hungarian patients with Pompe’s disease
Benjámin Bereznai(Ludwig-Maximilians-Universität München), Mária Judit Molnár(Istituto delle Scienze Neurologiche di Bologna), Ágnes Herczegfalvi, Katalin Várdi Visy(Országos Gyógyintézeti Központ), Zsolt Illés(Universität Hamburg), Anita Trauninger(University of Pecs), Katalin Szakszon(Boston Children's Hospital), I György(University of Debrecen), Zsuzsanna Almássy(Boston Children's Hospital), Endre Pál(University of Pecs)
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