Characterization of Leber Congenital Amaurosis-associated NMNAT1 Mutants

Yo Sasaki(SHOWA Medical University), Jeffrey Milbrandt(James S. McDonnell Foundation), Zachary Margolin(Washington University in St. Louis), Benjamin Borgo(Washington University in St. Louis), James J. Havranek(Washington University in St. Louis)
Journal of Biological Chemistry
May 28, 2015
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