Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

Roland W. Herzog(University of Pennsylvania), Edmund Y. Yang(Children's Hospital of Philadelphia), Linda B. Couto(Epigen Biosciences (United States)), J. Nathan Hagstrom(Children's Hospital of Philadelphia), Dan Elwell(University of North Carolina at Chapel Hill), Paul Fields(University of Pennsylvania), Melissa Burton(Epigen Biosciences (United States)), Dwight A. Bellinger(University of North Carolina at Chapel Hill), Marjorie S. Read(University of North Carolina at Chapel Hill), Kenneth M. Brinkhous(University of North Carolina at Chapel Hill), Gregory M. Podsakoff(Epigen Biosciences (United States)), Timothy C. Nichols(University of North Carolina at Chapel Hill), Gary J. Kurtzman(Epigen Biosciences (United States)), Katherine A. High(Human Gene Therapy Research Institute)
Nature Medicine
January 1, 1999
Cited by 562

Abstract


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