Leaderboards/Gene Therapy

Gene Therapy

Last updated May 19, 2026

Rising Stars

New and hot

Rising Stars Researchers

1
Xueliang Wang
Sun Yat-sen University
531 cit.
2
Giuseppe Caruso
European Institute of Oncology
435 cit.
3
Jerry R. Mendell
Nationwide Children's Hospital
432 cit.
4
Gustavo S. França
Institute for Systems Biology
432 cit.
5
Chris Bailey
The Francis Crick Institute
405 cit.
6
Luís Nunes
Uppsala University
393 cit.
7
Yan Zhuo
Nanchang University
358 cit.
8
Hui Wang
Fudan University
357 cit.
9
Tadepally Lakshmikanth
Karolinska Institutet
351 cit.
10
Jacob Witten
Massachusetts Institute of Technology
339 cit.

Rising Stars Papers

1
Fusobacterium nucleatum facilitates anti-PD-1 therapy in microsatellite stable colorectal cancer
Cancer Cell|2024
176 cit.
2
Ovarian Cancer
JAMA|2025
144 cit.
3
AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial
Nature Medicine|2024
143 cit.
4
Cellular adaptation to cancer therapy along a resistance continuum
Nature|2024
143 cit.
5
Origins and impact of extrachromosomal DNA
Nature|2024
134 cit.
6
Prognostic genome and transcriptome signatures in colorectal cancers
Nature|2024
130 cit.
7
Direct cytosolic delivery of siRNA via cell membrane fusion using cholesterol-enriched exosomes
Nature Nanotechnology|2024
142 cit.
8
Bilateral gene therapy in children with autosomal recessive deafness 9: single-arm trial results
Nature Medicine|2024
118 cit.
9
Immune system adaptation during gender-affirming testosterone treatment
Nature|2024
116 cit.
10
Artificial intelligence-guided design of lipid nanoparticles for pulmonary gene therapy
Nature Biotechnology|2024
112 cit.

Rising Stars Reagents

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Emerging Leaders

Gaining momentum

Emerging Leaders Researchers

1
Martin Jínek
ZHAW Zurich University of Applied Sciences
711 cit.
2
Katayoun Rezvani
The University of Texas MD Anderson Cancer Center
651 cit.
3
Wei Gu
Cancer Genetics (United States)
615 cit.
4
Karim Fizazi
Université Paris-Saclay
482 cit.
5
Linghua Wang
The University of Texas MD Anderson Cancer Center
467 cit.
6
Yilai Shu
Fudan University
465 cit.
7
William C. Cho
Hospital Authority
433 cit.
8
Matthew R. Nelson
Deerfield (United States)
419 cit.
9
Debyani Chakravarty
Memorial Sloan Kettering Cancer Center
379 cit.
10
Nir Hacohen
Broad Institute
323 cit.

Emerging Leaders Papers

1
Past, present, and future of CRISPR genome editing technologies
Cell|2024
474 cit.
2
Safety, efficacy and determinants of response of allogeneic CD19-specific CAR-NK cells in CD19+ B cell tumors: a phase 1/2 trial
Nature Medicine|2024
434 cit.
3
Understanding the complexity of p53 in a new era of tumor suppression
Cancer Cell|2024
410 cit.
4
Talazoparib plus enzalutamide in men with first-line metastatic castration-resistant prostate cancer (TALAPRO-2): a randomised, placebo-controlled, phase 3 trial
The Lancet|2023
482 cit.
5
Pan-cancer T cell atlas links a cellular stress response state to immunotherapy resistance
Nature Medicine|2023
467 cit.
6
AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial
The Lancet|2024
310 cit.
7
Interplay of oxidative stress, cellular communication and signaling pathways in cancer
Cell Communication and Signaling|2024
346 cit.
8
Refining the impact of genetic evidence on clinical success
Nature|2024
279 cit.
9
Quantifying the Expanding Landscape of Clinical Actionability for Patients with Cancer
Cancer Discovery|2023
379 cit.
10
Dictionary of immune responses to cytokines at single-cell resolution
Nature|2023
323 cit.

Emerging Leaders Reagents

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All-Time Leaders

The canon

All-Time Leaders Researchers

1
Louis M. Staudt
National Cancer Institute
29.8k cit.
2
Stephen Friend
Rosetta Stone (United States)
28.8k cit.
3
Matthew Meyerson
Broad Institute
28.2k cit.
4
D. Neil Hayes
University of North Carolina at Chapel Hill
23.1k cit.
5
Pier Paolo Pandolfi
Beth Israel Deaconess Medical Center
23k cit.
6
Alan Ashworth
Breast Cancer Now
19.9k cit.
7
Jean‐Paul Behr
Laboratoire de Chimie
18.6k cit.
8
Kenneth W. Kinzler
Howard Hughes Medical Institute
17.5k cit.
9
Jennifer A. Pietenpol
Vanderbilt University
16.4k cit.
10
Hiroyuki Mano
Japan Science and Technology Agency
16.2k cit.

All-Time Leaders Papers

1
Distinct types of diffuse large B-cell lymphoma identified by gene expression profiling
Nature|2000
9.9k cit.
2
Gene expression profiling predicts clinical outcome of breast cancer
Nature|2002
9.6k cit.
3
<i>EGFR</i> Mutations in Lung Cancer: Correlation with Clinical Response to Gefitinib Therapy
Science|2004
9.4k cit.
4
Integrated genomic analyses of ovarian carcinoma
Nature|2011
8.1k cit.
5
Integrated Genomic Analysis Identifies Clinically Relevant Subtypes of Glioblastoma Characterized by Abnormalities in PDGFRA, IDH1, EGFR, and NF1
Cancer Cell|2010
7.7k cit.
6
A ceRNA Hypothesis: The Rosetta Stone of a Hidden RNA Language?
Cell|2011
7.7k cit.
7
Targeting the DNA repair defect in BRCA mutant cells as a therapeutic strategy
Nature|2005
6.6k cit.
8
The Clonal Evolution of Tumor Cell Populations
Science|1976
6.5k cit.
9
Comprehensive molecular characterization of gastric adenocarcinoma
Nature|2014
6.5k cit.
10
A versatile vector for gene and oligonucleotide transfer into cells in culture and in vivo: polyethylenimine.
Proceedings of the National Academy of Sciences|1995
6.2k cit.

All-Time Leaders Reagents

Coming soon

Indexing Gene Therapy Reagents

Citation data for reagents in this field is currently compiling.