O.28Safety and tolerability of suvodirsen (WVE-210201) in patients with Duchenne muscular dystrophy: results from a phase 1 clinical trialKathryn R. Wagner, Michael Panzara, H. Phan et al.|Neuromuscular Disorders|2019Cited by 4
EP.83Design of a Phase 2/3 randomized controlled trial of suvodirsen (WVE-210201) in patients with Duchenne muscular dystrophy amenable to exon 51 skippingKathryn R. Wagner, Michael Panzara, E. Niks et al.|Neuromuscular Disorders|2019Cited by 1