COHORT 1-4 RESULTS FROM A PHASE 1/2 CLINICAL TRIAL OF AN AAV8-MEDIATED LIVER-DIRECTED GENE THERAPY IN ADULTS WITH GLYCOGEN STORAGE DISEASE TYPE IA (GSDIA)David Rodriguez‐Buritica, Eric Crombez, Maria-Luz Couce Pico et al.|Molecular Genetics and Metabolism|2022Cited by 1