Mitapivat Improves Ineffective Erythropoiesis and Reduces Iron Overload in Patients with Pyruvate Kinase DeficiencyEduard J. van Beers, Kevin H.M. Kuo, Hanny Al‐Samkari et al.|Blood|2021Cited by 3
Bone Mineral Density Remains Stable in Pyruvate Kinase Deficiency Patients Receiving Long-Term Treatment with MitapivatHanny Al‐Samkari, Eduard J. van Beers, Marta Morado et al.|Blood|2021Cited by 3
Bone mineral density in adult patients with pyruvate kinase deficiency on long-term mitapivat treatmentHanny Al‐Samkari, Eduard J. van Beers, Rachael F. Grace et al.|Haematologica|2023Cited by 2
Comorbidities and complications in adult and paediatric patients with pyruvate kinase deficiency: Analysis from the Peak RegistryAndreas Glenthøj, Paola Bianchi, Rachael F. Grace et al.|British Journal of Haematology|2024Cited by 2