<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1S. Hacein-Bey-Abina, Marina Cavazzana, N. M. Wulffraat et al.|Science|2003Cited by 3.5k
Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 DiseaseMarina Cavazzana, Alain Fischer, Salima Hacein‐Bey et al.|Science|2000Cited by 2.6k