A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase DeficiencyBarbara K. Burton, Anthony Quinn, Patrick Deegan et al.|New England Journal of Medicine|2015Cited by 244
The natural history of primary sclerosing cholangitis in 781 children: A multicenter, international collaborationMark Deneau, M. Kyle Jensen, Wael El‐Matary et al.|Hepatology|2017Cited by 224
Gamma Glutamyltransferase Reduction Is Associated With Favorable Outcomes in Pediatric Primary Sclerosing CholangitisMark Deneau, Tamir Miloh, Cara L. Mack et al.|Hepatology Communications|2018Cited by 47
The Sclerosing Cholangitis Outcomes in Pediatrics (SCOPE) Index: A Prognostic Tool for ChildrenMark Deneau, Nisreen Soufi, Cara L. Mack et al.|Hepatology|2020Cited by 43