Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with PolyneuropathyLaura Obici, Conceição de Azevedo Coutinho, Senda Ajroud‐Driss et al.|Neurology and Therapy|2023Cited by 21
In vivo CRISPR/Cas9 editing of the TTR gene with NTLA-2001 in patients with transthyretin amyloidosis- dose selection considerationsEdward Gane, Gillmore Julian, Justin Kao et al.|Journal of Hepatology|2022Cited by 5